"May I ask, what you would do if you had Nephrotic Syndrome resistant to other drug therapy and your only hope was an expensive drug or an expensive organ replacement/dialysis. And what would you do if your 18-year-old daughter gets diagnosed with a rare form of Nephrotic Syndrome and the choice is to use drugs that will cause infertility for life and possible blood cancers down the road or use an expensive drug with minimum side effects?"