Story highlights Hemophilia is a hereditary genetic condition

Patients do not have the gene allowing blood to clot

There is no known permanent cure

New gene-therapy trial finds long-term cure

London (CNN) A gene-therapy trial by London researchers has seen remarkable success in finding a long-term cure for hemophilia A.

The trial, by researchers at Barts Health NHS (National Health Service) Trust and Queen Mary University of London, used gene therapy to inject one dose of a missing gene in patients with the condition, and the gene continued functioning in the body for more than a year.

This is the first successful gene therapy to treat the condition.

Hemophilia is a hereditary genetic disorder, mostly affecting men, causing people to have low levels of clotting factor VIII, needed for their blood to clot.

Lack of the protein factor results in excessive bleeding from even minor injuries and can cause internal bleeding, which is life-threatening.

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