This page tracks new and upcoming treatment options for Charcot-Marie-Tooth disease (CMT). What’s in development? What’s promising? What’s available soon? Current topics include PXT3003, VM202 (Engensis), IFB-088 (Sephin1), HDAC6 inhibitors, SW-100, SARM1 inhibitors, ACE-083 , NTF3, gene therapy, PMP22, and more.

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